Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study

Author:

Howard James F,Utsugisawa Kimiaki,Benatar Michael,Murai Hiroyuki,Barohn Richard J,Illa Isabel,Jacob Saiju,Vissing John,Burns Ted M,Kissel John T,Muppidi Srikanth,Nowak Richard J,O'Brien Fanny,Wang Jing-Jing,Mantegazza Renato,Mazia Claudio Gabriel,Wilken Miguel,Ortea Carolina,Saba Juliet,Rugiero Marcelo,Bettini Mariela,Vidal Gonzalo,Garcia Alejandra Dalila,Lamont Phillipa,Leong Wai-Kuen,Boterhoven Heidi,Fyfe Beverly,Roberts Leslie,Jasinarachchi Mahi,Willlems Natasha,Wanschitz Julia,Löscher Wolfgang,De Bleecker Jan,Van den Abeele Guy,de Koning Kathy,De Mey Katrien,Mercelis Rudy,Wagemaekers Linda,Mahieu Delphine,Van Damme Philip,Smetcoren Charlotte,Stevens Olivier,Verjans Sarah,D'Hondt Ann,Tilkin Petra,Alves de Siqueira Carvalho Alzira,Hasan Rosa,Dias Brockhausen Igor,Feder David,Ambrosio Daniel,Melo Ana Paula,Rocha Rosana,Rosa Bruno,Veiga Thabata,Augusto da Silva Luiz,Gonçalves Geraldo Jordana,da Penha Morita Ananias Maria,Nogueira Coelho Erica,Paiva Gabriel,Pozo Marina,Prando Natalia,Dada Martineli Torres Debora,Fernanda Butinhao Cristiani,Coelho Erica,Renata Cubas Volpe Luciana,Duran Gustavo,Gomes da Silva Tamires Cristina,Otavio Maia Gonçalves Luiz,Pazetto Lucas Eduardo,Souza Duca Luciana,Suriane Fialho Tomás Augusto,Gheller Friedrich Maurício André,Guerreiro Alexandre,Mohr Henrique,Pereira Martins Maurer,da Cruz Pacheco Daiane,Macagnan Ana Paula,de Cassia Santos Aline,Bulle Oliveira Acary Souza,Amaral de Andrade Ana Carolina,Annes Marcelo,Cavalcante Lino Valeria,Pinto Wladimir,Miranda Carolina,Carrara Fernanda,Souza Iandra,Genge Angela,Massie Rami,Campbell Natasha,Bril Vera,Katzberg Hans,Soltani Mehran,Ng Eduardo,Siddiqi Zaeem,Phan Celile,Blackmore Derrick,Vohanka Stanislav,Bednarik Josef,Chmelikova Magda,Cierny Marek,Toncrova Stanislava,Junkerova Jana,Kurkova Barbora,Reguliova Katarina,Zapletalova Olga,Pitha Jiri,Novakova Iveta,Tyblova Michaela,Wolfova Marcela,Jurajdova Ivana,Andersen Henning,Harbo Thomas,Vinge Lotte,Mogensen Anita,Højgaard Joan,Witting Nanna,Autzen Anne Mette,Pedersen Jane,Färkkilä Markus,Atula Sari,Nyrhinen Anne,Erälinna Juha-Pekka,Laaksonen Mikko,Oksaranta Olli,Eriksson Jaana,Harrison Tuula,Desnuelle Claude,Sacconi Sabrina,Soriani Marie-Hélène,Decressac Sonia,Moutarde Julie,Lahaut Pauline,Solé Guilhem,Le Masson Gwendal,Wielanek-Bachelet Anne-Cécile,Gaboreau Morgane,Moreau Caroline,Wilson Amy,Vial Christophe,Bouhour Françoise,Gervais-Bernard Helene,Merle Hélène,Hourquin Caroline,Lacour Arnaud,Outteryck Olivier,Vermersch Patrick,Zephir Hélène,Millois Edouard,Deneve Michel,Deruelle Fabienne,Schoser Benedikt,Wenninger Stephan,Stangel Martin,Alvermann Sascha,Gingele Stefan,Skripuletz Thomas,Suehs Kurt-Wolfram,Trebst Corinna,Fricke Karin,Papagiannopoulos Sotirios,Bostantzopoulou Sevasti,Vlaikidis Nicholas,Zampaki Martha,Papadopoulou Nikoletta,Mitsikostas Dimos-Dimitrios,Kasioti Eleni,Mitropoulou Efstathia,Charalambous Despoina,Rozsa Csilla,Horvath Melinda,Lovas Gabor,Matolcsi Judit,Szabo Gyorgyi,Szabadosne Brigitta,Vecsei Laszlo,Dezsi Livia,Varga Edina,Konyane Monika,Gross Bella,Azrilin Olga,Greenbereg Nelly,Bali Kuperman Hila,Antonini Giovanni,Garibaldi Matteo,Morino Stefania,Troili Fernanda,Di Pasquale Antonella,Filla Alessandro,Costabile Teresa,Marano Enrico,Sacca Francesco,Marsil Angela,Puorro Giorgia,Maestri Tassoni Michelangelo,De Rosa Anna,Bonanno Silvia,Antozzi Carlo,Maggi Lorenzo,Campanella Angela,Angelini Corrado,Cudia Paola,Pegoraro Valentina,Pinzan Elena,Bevilacqua Francesca,Orrico Daniele,Bonifati Domenico Marco,Evoli Amelia,Alboini Paolo Emilio,D'Amato Valentina,Iorio Raffaele,Inghilleri Maurizio,Fionda Laura,Frasca Vittorio,Giacomelli Elena,Gori Maria,Lopergolo Diego,Onesti Emanuela,Gabriele Maria,Patti Francesco,Salvatore Caramma Andrea,Messina Silvia,Reggio Ester,Caserta Cinzia,Uzawa Akiyuki,Kanai Tetsuya,Mori Masahiro,Kaneko Yoko,Kanzaki Akiko,Kobayashi Eri,Masaki Katsuhisa,Matsuse Dai,Matsushita Takuya,Uehara Taira,Shimpo Misa,Jingu Maki,Kikutake Keiko,Nakamura Yumiko,Sano Yoshiko,Nagane Yuriko,Kamegamori Ikuko,Fujii Yuko,Futono Kazumi,Tsuda Tomoko,Saito Yuka,Suzuki Hidekazu,Morikawa Miyuki,Samukawa Makoto,Kamakura Sachiko,Shiraishi Hirokazu,Mitazaki Teiichiro,Motomura Masakatsu,Mukaino Akihiro,Yoshimura Shunsuke,Asada Shizuka,Kobashikawa Tomomi,Koga Megumi,Maeda Yasuko,Takada Kazumi,Takada Mihoko Takada,Yamashita Yumi,Yoshida Seiko,Suzuki Yasushi,Akiyama Tetsuya,Narikawa Koichi,Tsukita Kenichi,Meguro Fumie,Fukuda Yusuke,Sato Miwako,Matsuo Hidenori,Fukudome Takayasu,Gondo Yuichiro,Maeda Yasuhiro,Nagaishi Akiko,Nakane Shunya,Okubo Yoshinori,Okumura Meinoshin,Funaka Soichiro,Kawamura Tomohiro,Makamori Masayuki,Takahashi Masanori,Hasuike Tomoya,Higuchi Eriko,Kobayashi Hisako,Osakada Kaori,Taichi Namie,Tsuda Emiko,Hayashi Takashi,Hisahara Shin,Imai Tomihiro,Kawamata Jun,Murahara Takashi,Saitoh Masaki,Shimohama Shun,Suzuki Shuichiro,Yamamoto Daisuke,Konno Shingo,Imamura Tomomi,Inoue Masashi,Murata Mayumi,Nakazora Hiroshi,Nakayama Ritsu,Ikeda Yasuko,Ogawa Miki,Shirane Maoko,Kanda Takashi,Kawai Motoharu,Koga Michiaki,Ogasawara Junichi,Omoto Masatoshi,Sano Yasuteru,Arima Hideki,Fukui Sachie,Shimose Shigemi,Shinozaki Hirokazu,Watanabe Masanori,Yoshikawa Chieko,van der Kooi Anneke,de Visser Marianne,Gibson Tamar,Maessen Jos,de Baets Marc,Faber Catherine,Keijzers Maria Johanna,Miesen Monique,Kostera-Pruszczyk Anna,Kaminska Anna,Kim Byung-Jo,Lee Chang Nyoung,Koo Yong Seo,Seok Hung Youl,Kang Hoo Nam,Ra HyeJin,Kim Byoung Joon,Cho Eun Bin,Lee HyeLim,Min Ju-Hong,Seok Jinmyoung,Koh Da Yoon,Kwon JuYoung,Lee JiEun,Park SangAe,Hong Yoon-Ho,Lim Jae-Sung,Kim MiRi,Kim Seung Min,Kim Yool-hee,Lee Hyung Seok,Shin Ha Young,Hwang Eun Bi,Shin MiJu,Sazonov Denis,Yarmoschuk Asya,Babenko Larisa,Malkova Nadezhda,Melnikova Anna,Korobko Denis,Kosykh Evgeniya,Pokhabov Dmitry,Nesterova Yulia,Abramov Vladislav,Balyazin Victor,Casasnovas Pons Carlos,Alberti Aguilo Maria,Homedes-Pedret Christian,Palacios Natalia Julia,Lazaro Ana,Diez Tejedor Exuperio,Fernandez-Fournier Mireya,Lopez Ruiz Pedro,Rodriguez de Rivera Francisco Javier,Salvado Figueras Maria,Gamez Josep,Salvado Maria,Cortes Vicente Elena,Diaz-Manera Jordi,Querol Gutierrez Luis,Rojas Garcia Ricardo,Vidal Nuria,Arribas-Ibar Elisabet,Piehl Fredrik,Hietala Albert,Bjarbo Lena,Lindberg Christopher,Jons Daniel,Andersson Blanka,Sengun Ihsan,Ozcelik Pinar,Tuga Celal,Ugur Muzeyyen,Boz Cavit,Altiparmak Didem,Gazioglu Sibel,Ozen Aydin Cigdem,Erdem-Ozdamar Sevim,Bekircan-Kurt Can Ebru,Yilmaz Ezgi,Acar Nazire Pinar,Caliskan Yagmur,Efendi Husnu,Aydinlik Seda,Cavus Hakan,Semiz Cansu,Tun Ozlem,Terzi Murat,Dogan Baki,Onar Musa Kazim,Sen Sedat,Cavdar Tugce Kirbas,Norwood Fiona,Dimitriou Aikaterini,Gollogly Jakit,Mahdi-Rogers Mohamed,Seddigh Arshira,Maier Gal,Sohail Faisal,Sathasivam Sivakumar,Arndt Heike,Davies Debbie,Watling Dave,Rivner Michael,Hartmann J. Edward,Quarles Brandy,Smalley Nicole,Amato Anthony,Cochrane Thomas,Salajegheh Mohammed,Roe Kristen,Amato Katherine,Toska Shirli,Wolfe Gil,Silvestri Nicholas,Patrick Kara,Zakalik Karen,Katz Jonathan,Miller Robert,Engel Marguerite,Bravver Elena,Brooks Benjamin,Plevka Sarah,Burdette Maryanne,Sanjak Mohammad,Kramer Megan,Nemeth Joanne,Schommer Clara,Juel Vern,Guptill Jeffrey,Hobson-Webb Lisa,Beck Kate,Carnes Donna,Loor John,Anderson Amanda,Lange Dale,Agopian Eliz,Goldstein Jonathan,Manning Erin,Kaplan Lindsay,Holzberg Shara,Kassebaum Nicole,Pascuzzi Robert,Bodkin Cynthia,Kincaid John,Snook Riley,Guinrich Sandra,Micheels Angela,Chaudhry Vinay,Corse Andrea,Mosmiller Betsy,Ho Doreen,Srinivasan Jayashri,Vytopil Michael,Ventura Nicholas,Scala Stephanie,Carter Cynthia,Donahue Craig,Herbert Carol,Weiner Elaine,McKinnon Jonathan,Haar Laura,McKinnon Naya,Alcon Karan,Daniels Kevin,Sattar Nadia,Jeffery Dennis,McKenna Kaitlyn,Guidon Amanda,David William,Dheel Christina,Levine-Weinberg Mark,Nigro Catherine,Simpson Ericka,Appel Stanley H,Lai Eugene,Lay, Jr Luis,Pleitez Milvia,Halton Sharon,Faigle Casey,Thompson Lisa,Sivak Mark,Shin Susan,Bratton Joan,Jacobs Daniel,Brown Gavin,Bandukwala Ibrez,Brown Morris,Kane Jennifer,Blount Ira,Freimer Miriam,Hoyle J. Chad,Agriesti Julie,Khoury Julie,Marburger Tessa,Kaur Harpreet,Dimitrova Diana,Mellion Michelle,Sachs George,Crabtree Brigid,Keo Roseann,Perez Ele Kim,Taber Sandra,Gilchrist James,Andoin Angela,Darnell Taylor,Goyal Neelam,Sakamuri Sarada,So Yuen T,Welsh Lesly Welsh,Bhavaraju-Sanka Ratna,Tobon Gonzalez Alejandro,Jones Floyd,Saklad Amy,Nations Sharon,Trivedi Jaya,Hopkins Steve,Kazamel Mohamed,Alsharabati Mohammad,Lu Liang,Mumfrey-Thomas Sandi,Woodall Amy,Richman David,Butters Janelle,Lindsay Molly,Mozaffar Tahseen,Cash Tiyonnoh,Goyal Namita,Roy Gulmohor,Mathew Veena,Maqsood Fatima,Minton Brian,Jones H. James,Rosenfeld Jeffrey,Garcia Rebekah,Garcia Sonia,Echevarria Laura,Pulley Michael,Aranke Shachie,Berger Alan Ross,Shah Jaimin,Shabbir Yasmeen,Smith Lisa,Varghese Mary,Gutmann Laurie,Gutmann Ludwig,Swenson Andrea,Olalde Heena,Hafer-Macko Charlene,Kwan Justin,Zilliox Lindsay,Callison Karen,DiSanzo Beth,Naunton Kerry,Bilsker Martin,Sharma Khema,Reyes Eliana,Cooley Anne,Michon Sara-Claude,Steele Julie,Karam Chafic Karam,Chopra Manisha,Bird Shawn,Kaufman Jacob,Gallatti Nichole,Vu Tuan,Katzin Lara,McClain Terry,Harvey Brittany,Hart Adam,Huynh Kristin,Beydoun Said,Chilingaryan Amaiak,Droker Brian,Lin Frank,Shah Akshay,Tran Anh,Akhter Salma,Malekniazi Ali,Tandan Rup,Hehir Michael,Waheed Waqar,Lucy Shannon,Weiss Michael,Distad Jane,Downing Sharon,Strom Susan,Lisak Robert,Bernitsas Evanthia,Khan Omar,Kumar Sriwastava Shitiz,Tselis Alexandros,Jia Kelly,Bertorini Tulio,Arnold Thomas,Henderson Kendrick,Pillai Rekha,Liu Ye,Wheeler Lauren,Hewlett Jasmine,Vanderhook Mollie,Dicapua Daniel,Keung Benison,Kumar Aditya,Patwa Huned,Robeson Kimberly,Nye Joan,Vu Hong

Publisher

Elsevier BV

Subject

Neurology (clinical)

Reference40 articles.

1. Clinical characteristics of refractory myasthenia gravis patients;Suh;Yale J Biol Med,2013

2. Induction intravenous cyclophosphamide followed by maintenance oral immunosuppression in refractory myasthenia gravis;Buzzard;Muscle Nerve,2015

3. International consensus guidance for management of myasthenia gravis: executive summary;Sanders;Neurology,2016

4. Clinical and economic burden of refractory generalized myasthenia gravis in the United States;Engel-Nitz;J Neuromuscul Dis,2016

5. Antibody to acetylcholine receptor in myasthenia gravis. Prevalence, clinical correlates, and diagnostic value;Lindstrom;Neurology,1976

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号  京ICP备18003416号-3