Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study

Author:

Adams David,Polydefkis Michael,González-Duarte Alejandra,Wixner Jonas,Kristen Arnt V,Schmidt Hartmut H,Berk John L,Losada López Inés Asunción,Dispenzieri Angela,Quan Dianna,Conceição Isabel M,Slama Michel S,Gillmore Julian D,Kyriakides Theodoros,Ajroud-Driss Senda,Waddington-Cruz Márcia,Mezei Michelle M,Planté-Bordeneuve Violaine,Attarian Shahram,Mauricio Elizabeth,Brannagan Thomas H,Ueda Mitsuharu,Aldinc Emre,Wang Jing Jing,White Matthew T,Vest John,Berber Erhan,Sweetser Marianne T,Coelho Teresa,Vita Giuseppe,Rizzo Vincenzo,Russo Massimo,Mazzeo Anna,Gentile Luca,Berk John L,Brueckner Caitlin,Lazzari Victoria,Wiesman Janice,DeLong Douglas,Victory Jennifer,Dalton James,May John,Gilmore Catherine,Attarian Shahram,Diallo Saran,Delmont Emilien,Pouget Jean,Verschueren Annie,Grapperon Aude-Marie,Campana-Salort Emmanuelle,Conceição Isabel M,Lopes Ana,Lamas Filipa,Neves Carlos,Castro Jose,Pereira Pedro,Castro Isabel,Franco Ana,Santos Miguel Oliveira,de Azevedo Coutinho Conceição,Falcao de Campos Catarina,Coelho Teresa,Hipólito Reis Antonio,Correia Nuno,Perez Javier M,Martins da Silva Ana,Alves Cristina,Cardoso Marcio,Valdrez Katia,Monte Julia R,Pessoa Bernardete,Guimaraes Nadia,Freitas Monica,Ramalho Joana,Ferreira Natalia,Kuzume Daisuke,Tard Celine,Waucquier Nawal,Rougeaux Isabelle,Brice Sylvie,Kasprzyk Emmanuelle,Elrezzi Elise,Meguig Sayah,Hachulla Eric,Gauvain Clement,Migaud-Chervy Maria-Claire,Deplanque Dominique,Jozefowicz Elsa,Lebellec Loic,Adams David,Balaya-Gouraya Line,Jehan Lacour Nathalie,Bournane Halima,Martin Nathalie,Elabed Mongia,Sacko Niamey,Boubrit Yasmine,Gaouar Amina,Rakotondratafika Fetra,Théaudin-Saliou Marie,Cauquil-Michon Cécile,Labeyrie Celine,Not Adeline,Al-Salameh Abdallah,Lecoq Anne-Lise,Stephant Maeva,Echaniz-Laguna Andoni,Becquemont Laurent,Beaudonnet Guillemette,Algalarrondo Vincent,Eliahou Ludivine,Slama Michel S,Rousseau Antoine,Signate Aissatou,Berthelot Emeline,Inamo Jocelyn,Planté-Bordeneuve Violaine,Vervoitte Laetitia,Focseneanu Cecile,Gendre Thierry,Arrouasse Raphaele,Ayache Samar S.,Ernande Laura,Le Corvoisier Philippe,Salhi Hayet,Choumert Ariane,Ehinger Vincent,Ruiz Julie,Charlin Cyril,Megelin Thomas,Brannagan III Thomas H,Fayerman Raisy,Kim Arreum,Paras Allan,Gonzalez Leidy J,Tsang Steven,Wajnsztajn Fernanda,Shije Jeffrey,Ulane Christina,Kleyman Inna,Weimer Louis,Cioroiu Comana,Lambrianides Sakis,Abu-Manneh Rana,Zamba-Papanicolaou Eleni,Agathangelou Petros,Leonidou Eleni,Tada Satoshi,Fujita Akemi,Nagai Masahiro,Ando Rina,Hosokawa Yuko,Yamanishi Yuki,Overcash J. Scott,Giardino Elena,Boyer Leslie,Dang Lien,Le An,Nguyen Tyler,Giang Lien,Sellers Peter,Tran Leyla,Truong Nghi,Vinas Maita,Hrkman Nicole,Miller Sarah,Nguyen David,Smith Ashley,Pu Helen,Li Steve,Vuong Thao,Dioso Holly,Green Sinikka,Lee Kia,Chu Hanh,Waters Michael,Coskun Derya J,Zepeda Karla A,O'Riordan William,Obici Laura,Cortese Andrea,Lozza Alessandro,Merlini Giampaolo,Rosti Vittorio,Sabatelli Mario,Bisogni Giulia,Bernardo Daniela,Luigetti Marco,Di Paolantonio Andrea,Guglielmino Valeria,Bisogni Giulia,Romano Angela,Nienhuis Hans,Bulthuis-Kuiper Janita,Kristen Arnt V,Gerk Olga,Ulbricht Hannah,Taylor Lenka,Meyle Eva,Kleinschmidt Natalia,Meyrath David,Noe-Schwenn Simone,Meng Ulrike,Bauer Ralf,aus dem Siepen Fabian,Hein Selina,Takahashi Tetsuya,Oshita Tomohiko,Koujin Yoko,Neshige Shuichiro,Nezu Tomohisa,Segawa Akiko,Ueno Hiroki,Morino Hiroyuki,Campistol Josep M,Rodas Marin Lida Maria,Blasco Pelicano Josep Miquel,Dávila Lucía Galán,Palacios Marta,Pytel Cordoba Vanesa,Guerrero Sola Antonio,Horga Alejandro,García Feijoo Julián,Perez de Isla Leopoldo,Marques Júnior Wilson,Moscardini Mariana,Litcanov Debora Cristina,Viera Lima Ana Flavia,Rodrigues Leonardo,Marques Coutinho Barbara,Moreira Carolina Lavigne,Daccach Marques Vanessa,Munoz Beamud Francisco,Gragera Martínez Álvaro,Borrachero Cristina,Losada López Inés Asunción,Cisneros Barroso Eugenia,Rodríguez Rodríguez Adrián,Sanz Monica,Rigo Oliver Elena,González Moreno Juan,Gamez Martinez Jose M,Descals Cristina,Uson Mercedes,Jose Vega Francisco,Figuerola Antoni,Montala Carles,Waddington-Cruz Márcia,Dias da Silva Moises,Gervais de Santa Rosa Renata,Pinto Luiz Felipe,Pinto Marcus Vinicius,Cardoso Berensztejn Amanda,Barroso Fabio,Lautre Andrea,Orellana Lucas G,González-Duarte Briseño Maria Alejandra,Cárdenas-Soto Karla,Jiménez López Brenda Poled,Pérez-Castañeda Sandra Lorena,Cantú Brito Carlos Gerardo,Rivera de la Parra David,Hernandez Reyes Jose Pablo,del Mar Saniger Alba Maria,Criollo Mora Elia,Parman Yesim,Rezzan Kus Jülide,Sahin Erdi,Serbest Nail G,Durmus Hacer,Cakar Arman,Tugal Tutkun Nuriye Ilknur,Karamursel Sacit,Elitok Ali,Sirin Inan Nermin G,Altinkurt Emre,Polydefkis Michael,Ye Jing,Allen Adriane C,Chaudhry Vinay,Jarrett Raquel,Bressler Neil,Burks Kathleen L,Liu Qingfeng,Khoshnoodi Mohammad,Judge Daniel P,Vista Geno,Shah Syed Mahmood,Hamaguchi Hirotoshi,Oda Junko,Fukase Emi,Taniguchi Ikuko,Oda Tetsuya,Endo Hironobu,Shimomura Masahiro,Katanazaka Kimitaka,Koto Shusuke,Nakano Takahiro,Scheid Christof,Zueiter Andreas,Pester Lars,Walter Doreen,Özdemir Betül,Frenzel Lukas F,Holtick Udo,Oh Jeeyoung,Kim Hee Jin,Shin Hyun Jin,Choi Kyomin,Yamashita Taro,Ueda Mitsuharu,Masuda Teruaki,Misumi Yohei,Ueda Akihiko,Nakahara Keiichi,Yorita Akiko,Tsuruhisa Seiko,Taniwaki Takayuki,Harada Masaya,Moritaka Taiga,Sakurada Naonori,Mauricio Elizabeth A,Baskin Amber,Dimberg Elliot,Dispenzieri Angela,Fonder Amie,Hobbs Miriam,Russell Stephen J,Dyck Peter,Gonsalves Wilson,Leung Nelson,Witzig Thomas E,Zeldenrust Steven R,Hwa Lisa,Kapoor Prashant,Kumar Shaji K,Lin Yi,Lust John A,Rajkumar Vincent S,Dingli David,Gertz Morie A,Go Ronald,Hayman Suzanne R,Dalia Samir,Carrillo Esmeralda,Gorevic Peter,Mason Garnette,Chao Chi-Chao,Lee Ming-Jen,Su Jen-Jen,Hsieh Sung-Tsang,Tsai Li-Kai,Yeh Shin-Joe,Yang Chih-Chao,Ajroud-Driss Senda Ajroud-Driss,Casey Patricia,Joslin Benjamin C,Freimer Miriam,Sankey Alison,Kenepp Amanda,Heintzman Sarah,LoRusso Samantha,Hokezu Youichi,Kim Byoung-Joon,Kim JuHyeon,Lee Ga Yeon,Cho Eun Bin,Jeon Eun-Seok,Min Ju-Hong,Seok Jin Myoung,Lee Hye Lim,Park Jae Hong,Sekijima Yoshiki,Miyazawa Chinatsu,Kato Nagaaki,Kishida Dai,Hineno Akiyo,Kodaira Minori,Yoshinaga Tsuneaki,Miyahara Teruyoshi,Imai Akira,Matsumoto Kazuhiko,Lin Kon-Ping,Lee Yi-Chung,Wixner Jonas,Falk Malin,Pilebro Bjorn,Suhr Ole,Lindqvist Per,Soderberg Karin,Pedrosa-Domellöf Fatima,Anan Intissar,Nordh Erik,Tournev Ivaylo,Zhelyazkova-Glaveeva Sashka,Cherneva Zheyna,Sarafov Staiko,Chamova Teodora,Cherninkova-Gopina Sylvia,Schmidt Hartmut H,Friebel Frauke,Zibert Andree,Mihailovic Natasa,Schubert Friederike,Vorona Elena,Lahme Larissa,Huesing-Kabar Anna,Schilling Matthias,Kabar Iyad,Gillmore Julian D,Martinez-Naharro Ana,Chacko Liza,Cohen Oliver,Law Steven,Rezk Tamer,Lachmann Helen J,Quan Dianna,Blume Brianna,Dixon Stacy,Low Soon Chai,Chan Soo Looi,Lim He Eng Li,Goh Khean Jin,Mezei Michelle M,Kraus Deborah,Jack Kristin,Wade N. Kevin,Lopate Glenn,Zwijack Brittany,Florence Julaine,Sommerville R. Brian,Stewart Graeme,Ryder Julie,Mekhael Linda,Taylor Mark,Suan Daniel,Wells Karen,Stone Paula,Wells Karen,Itoya Amenze,Owusu-Sekyere Mercy,Thai Desmond,Chahine Ilonah,Pedrosa Salve,Do Thi Hoa (Therese)

Publisher

Elsevier BV

Subject

Neurology (clinical)

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