Durability of Voretigene Neparvovec for Biallelic RPE65-Mediated Inherited Retinal Disease

Author:

Maguire Albert M.,Russell Stephen,Chung Daniel C.,Yu Zi-Fan,Tillman Amy,Drack Arlene V.,Simonelli Francesca,Leroy Bart P.,Reape Kathleen Z.,High Katherine A.,Bennett Jean

Publisher

Elsevier BV

Subject

Ophthalmology

Reference19 articles.

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2. Leber’s congenital amaurosis and the role of gene therapy in congenital retinal disorders;Sharif;Int J Ophthalmol,2017

3. Longitudinal and cross-sectional study of patients with early-onset severe retinal dystrophy associated with RPE65 mutations;Paunescu;Graefes Arch Clin Exp Ophthalmol,2005

4. Mutations in the RPE65 gene in patients with autosomal recessive retinitis pigmentosa or Leber congenital amaurosis;Morimura;Proc Natl Acad Sci U S A,1998

5. Optic-flow and egocentric-direction strategies in walking: central vs peripheral visual field;Turano;Vision Res,2005

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