Pegvaliase for the treatment of phenylketonuria: Results of a long-term phase 3 clinical trial program (PRISM)-Reference-Cited by-同舟云学术

Pegvaliase for the treatment of phenylketonuria: Results of a long-term phase 3 clinical trial program (PRISM)

Published:2018-05 Issue:1 Volume:124 Page:27-38
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Thomas Janet,Levy Harvey,Amato Stephen,Vockley Jerry^ORCID,Zori Roberto,Dimmock David,Harding Cary O.^ORCID,Bilder Deborah A.,Weng Haoling H.,Olbertz Joy,Merilainen Markus,Jiang Joy,Larimore Kevin^ORCID,Gupta Soumi,Gu Zhonghua,Northrup Hope

Funder

BioMarin Pharmaceutical Inc

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference40 articles.

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2. High phenylalanine levels directly affect mood and sustained attention in adults with phenylketonuria: a randomised, double-blind, placebo-controlled, crossover trial;ten Hoedt;J. Inherit. Metab. Dis.,2011

3. Systematic review and meta-analysis of neuropsychiatric symptoms and executive functioning in adults with phenylketonuria;Bilder;Dev. Neuropsychol.,2016

4. Quality of life in noncompliant adults with phenylketonuria after resumption of the diet;Bik-Multanowski;J. Inherit. Metab. Dis.,2008

5. Novato;Kuvan [package insert],2016

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