Growth advantage of corrected hepatocytes in a juvenile model of methylmalonic acidemia following liver directed adeno-associated viral mediated nuclease-free genome editing-Reference-Cited by-同舟云学术

Growth advantage of corrected hepatocytes in a juvenile model of methylmalonic acidemia following liver directed adeno-associated viral mediated nuclease-free genome editing

Published:2022-09 Issue:1-2 Volume:137 Page:1-8
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Venturoni Leah E.,Chandler Randy J.,Liao Jing,Hoffmann Victoria,Ramesh Nikhil,Gordo Susana,Chau Nelson,Venditti Charles P.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference43 articles.

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4. Methylmalonic and propionic acidemias: clinical management update;Fraser;Curr. Opin. Pediatr.,2016

5. Variable dietary management of methylmalonic acidemia: metabolic and energetic correlations;Hauser;Am. J. Clin. Nutr.,2011

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