The relationship between anti-idursulfase antibody status and safety and efficacy outcomes in attenuated mucopolysaccharidosis II patients aged 5years and older treated with intravenous idursulfase-Reference-Cited by-同舟云学术

The relationship between anti-idursulfase antibody status and safety and efficacy outcomes in attenuated mucopolysaccharidosis II patients aged 5years and older treated with intravenous idursulfase

Published:2013-11 Issue:3 Volume:110 Page:303-310
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Barbier A.J.,Bielefeld B.,Whiteman D.A.H.,Natarajan M.,Pano A.,Amato D.A.

Funder

Shire

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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3. Initial report from the Hunter Outcome Survey;Wraith;Genet. Med.,2008

4. Mortality and cause of death in mucopolysaccharidosis type II—a historical review based on data from the Hunter Outcome Survey (HOS);Jones;J. Inherit. Metab. Dis.,2009

5. Recognition and diagnosis of mucopolysaccharidosis II (Hunter syndrome);Martin;Pediatrics,2008

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