Pulmonary delivery of recombinant acid sphingomyelinase improves clearance of lysosomal sphingomyelin from the lungs of a murine model of Niemann

Pulmonary delivery of recombinant acid sphingomyelinase improves clearance of lysosomal sphingomyelin from the lungs of a murine model of Niemann–Pick disease

Published:2009-05 Issue:1 Volume:97 Page:35-42
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Ziegler Robin J.,Brown Claire,Barbon Christine M.,D’Angona Anne Marie,Schuchman Edward H.,Andrews Laura,Thurberg Beth L.,McPherson John M.,Karey Kenneth P.,Cheng Seng H.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference34 articles.

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3. Pulmonary involvement in Niemann–Pick disease: case report and literature review;Minai;Respir. Med.,2000

4. The natural history of type B Niemann–Pick disease: results from a 10-year longitudinal study;Wasserstein;Pediatrics,2004

5. Lung disease in Niemann–Pick disease;Guillemot;Pediatr. Pulmonol.,2007

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