Risk factors for severe clinical events in male and female patients with Fabry disease treated with agalsidase beta enzyme replacement therapy: Data from the Fabry Registry-Reference-Cited by-同舟云学术

Risk factors for severe clinical events in male and female patients with Fabry disease treated with agalsidase beta enzyme replacement therapy: Data from the Fabry Registry

Published:2016-09 Issue:1-2 Volume:119 Page:151-159
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Hopkin Robert J.^ORCID,Cabrera Gustavo,Charrow Joel,Lemay Roberta,Martins Ana Maria,Mauer Michael,Ortiz Alberto,Patel Manesh R.,Sims Katherine,Waldek Stephen,Warnock David G.,Wilcox William R.

Funder

Sanofi Genzyme

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference43 articles.

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3. Females with Fabry disease frequently have major organ involvement: lessons from the Fabry Registry;Wilcox;Mol. Genet. Metab.,2008

4. Fabry disease: progression of nephropathy, and prevalence of cardiac and cerebrovascular events before enzyme replacement therapy;Schiffmann;Nephrol. Dial. Transplant.,2009

5. Cardiovascular events in patients with Fabry disease natural history data from the Fabry registry;Patel;J. Am. Coll. Cardiol.,2011

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