Enzyme replacement therapy with galsulfase in 34 children younger than five years of age with MPS VI-Reference-Cited by-同舟云学术

Enzyme replacement therapy with galsulfase in 34 children younger than five years of age with MPS VI

Published:2013-05 Issue:1 Volume:109 Page:62-69
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Horovitz Dafne D.G.,Magalhães Tatiana S.P.C.,Acosta Angelina,Ribeiro Erlane M.,Giuliani Liane R.,Palhares Durval B.,Kim Chong A.,de Paula Ana Carolina,Kerstenestzy Marcelo,Pianovski Mara A.D.,Costa Maria Ione F.,Santos Francisca C.,Martins Ana Maria,Aranda Carolina S.,Neto Jordão Correa,Holanda Gervina Brady Moreira,Cardoso Laércio,da Silva Carlos A.B.,Bonatti Renata C.F.,Ribeiro Bethania F.R.,Rodrigues Maria do Carmo S.,Llerena Juan C.

Funder

BioMarin Pharmaceutical Inc

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference20 articles.

1. Mucopolysaccharidosis VI;Valayannopoulos;Orphanet J. Rare Dis.,2010

2. The mucopolysaccharidoses;Neufeld,2001

3. Mucopolysacharidoses type VI (Maroteaux Lamy Syndrome;Wraith,2007

4. Enzyme replacement therapy in mucopolysaccharidosis VI (Maroteaux-Lamy syndrome);Harmatz;J. Pediatr.,2004

5. Direct Comparison of Measures of Endurance, Mobility, and Joint Function During Enzyme-Replacement Therapy of Mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome): Results After 48 Weeks in a Phase 2 Open-Label Clinical Study of Recombinant Human N-Acetylgalactosamine 4-Sulfatase

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