Urinary glycosaminoglycans as a potential biomarker for evaluating treatment efficacy in subjects with mucopolysaccharidoses
Author:
Publisher
Elsevier BV
Subject
Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism
Reference51 articles.
1. Mucopolysaccharidoses;Cimaz;Curr. Rheumatol. Rep.,2014
2. The mucopolysaccharidoses;Neufeld,2001
3. Enzyme-replacement therapy in mucopolysaccharidosis I;Kakkis;N. Engl. J. Med.,2001
4. A phase II/III clinical study of enzyme replacement therapy with idursulfase in mucopolysaccharidosis II (Hunter syndrome);Muenzer;Genet. Med.,2006
5. Role of elosulfase alfa in mucopolysaccharidosis IVA;Regier;Appl. Clin. Genet.,2016
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