Long-term efficacy of hematopoietic stem cell transplantation on brain involvement in patients with mucopolysaccharidosis type II: A nationwide survey in Japan-Reference-Cited by-同舟云学术

Long-term efficacy of hematopoietic stem cell transplantation on brain involvement in patients with mucopolysaccharidosis type II: A nationwide survey in Japan

Published:2012-11 Issue:3 Volume:107 Page:513-520
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Tanaka Akemi,Okuyama Torayuki,Suzuki Yasuyuki,Sakai Norio,Takakura Hiromitsu,Sawada Tomo,Tanaka Toju,Otomo Takanobu,Ohashi Toya,Ishige-Wada Mika,Yabe Hiromasa,Ohura Toshihiro,Suzuki Nobuhiro,Kato Koji,Adachi Souichi,Kobayashi Ryoji,Mugishima Hideo,Kato Shunichi

Funder

Ministry, of Health, Labour and Welfare, Japan

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference27 articles.

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2. Cord-blood transplants from unrelated donors in patients with Hurler's syndrome;Staba;N. Engl. J. Med.,2004

3. Outcomes of hematopoietic stem cell transplantation for Hurler's syndrome in Europe: a risk factor analysis for graft failure;Boelens;Bone Marrow Transplant.,2007

4. Mucopolysaccharidosis I: management and treatment guidelines;Muenzer;Pediatrics,2009

5. Bone marrow transplantation in children with Hunter Syndrome: outcome after 7 to 17years;Guffon;J. Pediatr.,2009

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