Therapy for Gaucher disease: Don’t stop thinking about tomorrow-Reference-Cited by-同舟云学术

Therapy for Gaucher disease: Don’t stop thinking about tomorrow

Published:2007-02 Issue:2 Volume:90 Page:122-125
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Sidransky Ellen,LaMarca Mary E.,Ginns Edward I.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference31 articles.

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2. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources;Grabowski;Ann. Intern. Med.,1995

3. Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the gaucher registry;Weinreb;Am. J. Med.,2002

4. Acceleration of retarded growth in children with Gaucher disease after treatment with alglucerase;Kaplan;J. Pediatr.,1996

5. Delayed growth and puberty in patients with Gaucher disease type 1: natural history and effect of splenectomy and/or enzyme replacement therapy;Kauli;Isr. Med. Assoc. J.,2000

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