Enzyme replacement therapy in newborn mucopolysaccharidosis IVA mice: Early treatment rescues bone lesions?-Reference-Cited by-同舟云学术

Enzyme replacement therapy in newborn mucopolysaccharidosis IVA mice: Early treatment rescues bone lesions?

Published:2015-02 Issue:2 Volume:114 Page:195-202
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Tomatsu Shunji,Montaño Adriana M.,Oikawa Hirotaka,Dung Vu Chi,Hashimoto Amiko,Oguma Toshihiro,Gutiérrez Monica L.,Takahashi Tatsuo,Shimada Tsutomu,Orii Tadao,Sly William S.

Funder

Austrian MPS Society

National MPS Society

The Jacob Randall Foundation for Morquio

Bennett Foundation

International Morquio Organization

National Institutes of Health

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference51 articles.

1. Enzyme replacement therapy in a murine model of Morquio A syndrome;Tomatsu;Hum. Mol. Genet.,2008

2. Current and emerging treatments and surgical interventions for Morquio A syndrome: a review;Tomatsu;Res. Rep. Endocr. Disord.,2012

3. An update on the frequency of mucopolysaccharide syndromes in British Columbia;Lowry;Hum. Genet.,1990

4. Incidence of inborn errors of metabolism in British Columbia. 1969–1996;Applegarth;Pediatrics,2000

5. Incidence of the mucopolysaccharidoses in Northern Ireland;Nelson;Hum. Genet.,1997

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