In vitro functional correction of Hermansky–Pudlak Syndrome type-1 by lentiviral-mediated gene transfer-Reference-Cited by-同舟云学术

In vitro functional correction of Hermansky–Pudlak Syndrome type-1 by lentiviral-mediated gene transfer

Published:2015-01 Issue:1 Volume:114 Page:62-65
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Ikawa Yasuhiro,Hess Richard,Dorward Heidi,Cullinane Andrew R.,Huizing Marjan,Gochuico Bernadette R.,Gahl William A.,Candotti Fabio

Funder

National Human Genome Research Institute

National Institutes of Health

UNIL-CHUV

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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