UX007 for the treatment of long chain-fatty acid oxidation disorders: Safety and efficacy in children and adults following 24 weeks of treatment-Reference-Cited by-同舟云学术

UX007 for the treatment of long chain-fatty acid oxidation disorders: Safety and efficacy in children and adults following 24 weeks of treatment

Published:2017-04 Issue:4 Volume:120 Page:370-377
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Vockley J.^ORCID,Burton B.,Berry G.T.,Longo N.,Phillips J.,Sanchez-Valle A.,Tanpaiboon P.,Grunewald S.,Murphy E.,Humphrey R.,Mayhew J.,Bowden A.,Zhang L.,Cataldo J.,Marsden D.L.,Kakkis E.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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