Allogeneic Hematopoietic Stem Cell Transplantation in Thirty-Four Pediatric Cases of Mucopolysaccharidosis—A Ten-Year Report from the China Children Transplant Group-Reference-Cited by-同舟云学术

Allogeneic Hematopoietic Stem Cell Transplantation in Thirty-Four Pediatric Cases of Mucopolysaccharidosis—A Ten-Year Report from the China Children Transplant Group

Published:2016-11 Issue:11 Volume:22 Page:2104-2108
ISSN:1083-8791
Container-title:Biology of Blood and Marrow Transplantation
language:en
Short-container-title:Biology of Blood and Marrow Transplantation

Author:

Wang Jianmin,Luan Zuo,Jiang Hua,Fang Jianpei,Qin Maoquan,Lee Vincent,Chen Jing

Publisher

Elsevier BV

Subject

Transplantation,Hematology

Reference18 articles.

1. Targeting gene-modified hematopoietic cells to the central nervous system: use of green fluorescent protein uncovers microglial engraftment;Priller;Nat Med,2001

2. Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure;De Ru;Orphanet J Rare Dis,2011

3. Bone marrow transplantation as effective treatment of central nervous system disease in globoid cell leukodystrophy, mannosidosis, fucosidosis, aspartylglucosaminuria, Hurler, Maroteaux-Lamy, and Sly syndromes, and Gaucher disease type III;Krivit;Curr Opin Neurol,1999

4. Reversal of clinical features of Hurler's disease and biochemical improvement after treatment by bone-marrow transplantation;Hobbs;Lancet,1981

5. Mucopolysaccharidosis I: management and treatment guidelines;Muenzer;Pediatrics,2009

Cited by 54 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Health service utilization, economic burden and quality of life of patients with mucopolysaccharidosis in China;Orphanet Journal of Rare Diseases;2024-09-06

2. Reversal of SLE and hemophagocytic lymphohistiocytosis caused by lysinuric protein intolerance through allogeneic hematopoietic stem cell transplantation;Journal of Allergy and Clinical Immunology;2023-06

3. Ovarian tissue cryopreservation in the pediatric with rare diseases- experience from China’s first and the largest ovarian tissue cryobank;Frontiers in Endocrinology;2023-04-03

4. Individual Treatment Trials—Do Experts Know and Use This Option to Improve the Treatability of Mucopolysaccharidosis?;Pharmaceuticals;2023-03-09

5. Current and new therapies for mucopolysaccharidoses;Pediatrics & Neonatology;2023-02