Orphan drugs: major development challenges at the clinical stage-Reference-Cited by-同舟云学术

Orphan drugs: major development challenges at the clinical stage

Published:2019-03 Issue:3 Volume:24 Page:867-872
ISSN:1359-6446
Container-title:Drug Discovery Today
language:en
Short-container-title:Drug Discovery Today

Author:

Fonseca Diogo A.^ORCID,Amaral Inês,Pinto Ana Catarina,Cotrim Maria Dulce

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology

Reference42 articles.

1. Marketing authorisation of orphan medicines in Europe from 2000 to 2013;Hofer;Drug Discov. Today,2018

2. Orphan drugs: the regulatory environment;Franco;Drug Discov. Today,2013

3. Orphan drug development is progressing too slowly;Joppi;Br. J. Clin. Pharmacol.,2006

4. Regulation (EC) No. 141/2000 of the European Parliament and of the Council of 16 December 1999 on Orphan Medicinal Products;European Commission,1999

5. Orphan Drug Act, Public Law 97-414;US Congress,1983

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