Targeted gene therapy in human-induced pluripotent stem cells from a patient with primary hyperoxaluria type 1 using CRISPR/Cas9 technology-Reference-Cited by-同舟云学术

Targeted gene therapy in human-induced pluripotent stem cells from a patient with primary hyperoxaluria type 1 using CRISPR/Cas9 technology

Published:2019-10 Issue:4 Volume:517 Page:677-683
ISSN:0006-291X
Container-title:Biochemical and Biophysical Research Communications
language:en
Short-container-title:Biochemical and Biophysical Research Communications

Author:

Estève Julie,Blouin Jean-Marc,Lalanne Magalie,Azzi-Martin Lamia,Dubus Pierre,Bidet Audrey,Harambat Jérôme,Llanas Brigitte,Moranvillier Isabelle,Bedel Aurélie,Moreau-Gaudry François,Richard Emmanuel^ORCID

Funder

Institut National de la Santé et de la Recherche Médicale

Université de Bordeaux

Oxalosis and Hyperoxaluria Foundation

Association Française contre les Myopathies

Publisher

Elsevier BV

Subject

Cell Biology,Molecular Biology,Biochemistry,Biophysics

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