Validating New Symptom Emergence as a Patient-Centric Outcome Measure for PD Clinical Trials

Author:

Zou HaotianORCID,Stebbins Glenn T.ORCID,Simuni Tanya,Luo ShengORCID,Cedarbaum Jesse M.ORCID

Funder

Michael J. Fox Foundation for Parkinson's Research

Publisher

Elsevier BV

Reference27 articles.

1. Movement Disorder Society-Sponsored Revision of the Unified Parkinson's Disease Rating Scale (MDS-UPDRS): Scale Presentation and Clinimetric Testing Results;Goetz;Movement Disorders,2008

2. Progression of MDS-UPDRS Scores Over Five Years in De Novo Parkinson Disease from the Parkinson’s Progression Markers Initiative Cohort;Holden;Movement Disorders Clinical Practice,2018

3. C.E. O’Hanlon, C.M. Farmer, J. Ryan, N.C. Ernecoff, Clinical Outcome Assessments and Digital Health Technologies Supporting Clinical Trial Endpoints in Early Parkinson's Disease: Roundtable Proceedings and Roadmap for Research. 2023. The RAND Coroporation. https://www.rand.org/pubs/conf_proceedings/CFA2550-1.html

4. Longitudinal Change of Clinical and Biological Measures in Early Parkinson’s Disease: Parkinson’s Progression Markers Initiative Cohort;Simuni;Movement Disorders,2018

5. Does the MDS-UPDRS provide the precision to assess progression in early Parkinson’s disease? Learnings from the Parkinson’s progression marker initiative cohort;Regnault;Journal of Neurology,2019

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