In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery Methods-Reference-Cited by-同舟云学术

In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery Methods

Published:2019-09 Issue: Volume:17 Page:277-288
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Pattabhi Sowmya,Lotti Samantha N.,Berger Mason P.,Singh Swati,Lux Christopher T.,Jacoby Kyle,Lee Calvin,Negre Olivier,Scharenberg Andrew M.,Rawlings David J.

Funder

Seattle Children’s Research Institute, Program for Cell and Gene Therapy

NIH

bluebird bio, Inc.

Children’s Guild Association Endowed Chair in Pediatric Immunology

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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