A CAG repeat-targeting artificial miRNA lowers the mutant huntingtin level in the YAC128 model of Huntington's disease
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference53 articles.
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4. The contribution of somatic expansion of the CAG repeat to symptomatic development in Huntington’s disease: a historical perspective;Monckton;J. Huntingtons Dis.,2021
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