Exon Skipping in a Dysf-Missense Mutant Mouse Model-Reference-Cited by-同舟云学术

Exon Skipping in a Dysf-Missense Mutant Mouse Model

Published:2018-12 Issue: Volume:13 Page:198-207
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Malcher Jakub,Heidt Leonie,Goyenvalle Aurélie,Escobar Helena,Marg Andreas,Beley Cyriaque,Benchaouir Rachid,Bader Michael,Spuler Simone,García Luis,Schöwel Verena

Funder

German Research Foundation

International Research Training Group for Muscle Sciences “MyoGrad”

Helmholtz Association

Charité Universitätsmedizin Berlin

Duchenne Parent project France

Association Monégasque contre les Myopathies

Open Access Publication Fund

Charité – Universitätsmedizin Berlin

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference53 articles.

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2. Defective membrane repair in dysferlin-deficient muscular dystrophy;Bansal;Nature,2003

3. Sarcolemmal repair is a slow process and includes EHD2;Marg;Traffic,2012

4. Dysferlin and the plasma membrane repair in muscular dystrophy;Bansal;Trends Cell Biol.,2004

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