Repurposing Dantrolene for Long-Term Combination Therapy to Potentiate Antisense-Mediated DMD Exon Skipping in the mdx Mouse-Reference-Cited by-同舟云学术

Repurposing Dantrolene for Long-Term Combination Therapy to Potentiate Antisense-Mediated DMD Exon Skipping in the mdx Mouse

Published:2018-06 Issue: Volume:11 Page:180-191
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Wang Derek W.,Mokhonova Ekaterina I.,Kendall Genevieve C.,Becerra Diana,Naeini Yalda B.,Cantor Rita M.,Spencer Melissa J.,Nelson Stanley F.,Miceli M. Carrie

Funder

NIH

California Institute of Regenerative Medicine

UCLA Muscular Dystrophy Core Center

Center for Duchenne Muscular Dystrophy at UCLA

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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5. Hypernitrosylated ryanodine receptor calcium release channels are leaky in dystrophic muscle;Bellinger;Nat. Med.,2009

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