Prime editing optimized RTT permits the correction of the c.8713C>T mutation in DMD gene-Reference-Cited by-同舟云学术

Prime editing optimized RTT permits the correction of the c.8713C>T mutation in DMD gene

Published:2022-12 Issue: Volume:30 Page:272-285
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Happi Mbakam Cedric^ORCID,Rousseau Joel,Lu Yaoyao,Bigot Anne,Mamchaoui Kamel,Mouly Vincent,Tremblay Jacques P.^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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