Prime editing optimized RTT permits the correction of the c.8713C>T mutation in DMD gene

Author:

Happi Mbakam CedricORCID,Rousseau Joel,Lu Yaoyao,Bigot Anne,Mamchaoui Kamel,Mouly Vincent,Tremblay Jacques P.ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference39 articles.

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3. Age at onset of first signs or symptoms predicts age at loss of ambulation in Duchenne and Becker Muscular Dystrophy: Data from the MD STARnet;Ciafaloni;J. Pediatr. Rehabil. Med.,2016

4. The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review;Ryder;Orphanet J. Rare Dis.,2017

5. Global epidemiology of Duchenne muscular dystrophy: an updated systematic review and meta-analysis;Crisafulli;Orphanet J. Rare Dis.,2020

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