Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia-Reference-Cited by-同舟云学术

Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia

Published:2022-09 Issue: Volume:29 Page:551-562
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Lee Jeong Hyeon,Oh Hye-Kyung,Choi Beom Seok,Lee Ho Hyeon,Lee Kyu Jun,Kim Un Gi,Lee Jina,Lee Hyerim,Lee Geon Seong,Ahn Se Jun,Han Jeong Pil,Kim Seokjoong,Yeom Su Cheong,Song Dong Woo^ORCID

Funder

Korea Institute of Toxicology

National Research Foundation of Korea

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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