Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties-Reference-Cited by-同舟云学术

Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties

Published:2022-09 Issue: Volume:29 Page:955-968
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Chwalenia Katarzyna,Oieni Jacopo,Zemła Joanna,Lekka Małgorzata,Ahlskog Nina,Coenen-Stass Anna M.L.,McClorey Graham,Wood Matthew J.A.,Lomonosova Yulia,Roberts Thomas C.^ORCID

Funder

Medical Research Council

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference63 articles.

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5. Advances in oligonucleotide drug delivery;Roberts;Nat. Rev. Drug Discov.,2020

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