Genome Editing-Mediated Utrophin Upregulation in Duchenne Muscular Dystrophy Stem Cells
Author:
Funder
University of Pennsylvania Orphan Disease Center
Muscular Dystrophy Association, USA
NINDS
NIAMS
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference66 articles.
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2. A systematic review and meta-analysis on the epidemiology of Duchenne and Becker muscular dystrophy;Mah;Neuromuscul. Disord.,2014
3. Complete cloning of the Duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals;Koenig;Cell,1987
4. Dystrophin: the protein product of the Duchenne muscular dystrophy locus;Hoffman;Cell,1987
5. The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein;Koenig;Cell,1988
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