Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide-Reference-Cited by-同舟云学术

Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide

Published:2019-09 Issue: Volume:17 Page:601-614
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Kourkouta Eleni,Weij Rudie,González-Barriga Anchel,Mulder Melissa,Verheul Ruurd,Bosgra Sieto,Groenendaal Bas,Puoliväli Jukka,Toivanen Jussi,van Deutekom Judith C.T.,Datson Nicole A.

Funder

BioMarin

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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