Good news for the mdx mouse community: Improved dystrophin restoration after skipping mouse dystrophin exon 23
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference4 articles.
1. A cell-penetrating peptide enhances delivery and efficacy of phosphorodiamidate morpholino oligomers in mdx mice;Gan;Mol. Ther. Nucleic Acids,2022
2. A dystrophic Duchenne mouse model for testing human antisense oligonucleotides;Veltrop;PLoS One,2018
3. Magnesium in man: implications for health and disease;de Baaij;Physiol. Rev.,2015
4. Report of a TREAT-NMD/world Duchenne organisation meeting on dystrophin quantification methodology;Aartsma-Rus;J. Neuromuscul. Dis.,2019
Cited by 2 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Morpholino oligonucleotide-mediated exon skipping for DMD treatment: Past insights, present challenges and future perspectives;Journal of Biosciences;2023-10-11
2. The Dilemma of Choice for Duchenne Patients Eligible for Exon 51 Skipping The European Experience;Journal of Neuromuscular Diseases;2023-05-02
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