Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy-Reference-Cited by-同舟云学术

Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy

Published:2018-03 Issue: Volume:10 Page:376-386
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Azibani Feriel,Brull Astrid,Arandel Ludovic,Beuvin Maud,Nelson Isabelle,Jollet Arnaud,Ziat Esma,Prudhon Bernard,Benkhelifa-Ziyyat Sofia,Bitoun Marc,Lorain Stéphanie,Bonne Gisèle,Bertrand Anne T.

Funder

INSERM

Association Institut de Myologie

Sorbonne Université-Médecine

Centre National de la Recherche Scientifique

CURE-CMD Foundation

Andrés Marcio Foundation

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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5. Mutations in the gene encoding lamin A/C cause autosomal dominant Emery-Dreifuss muscular dystrophy;Bonne;Nat. Genet.,1999

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