Long-term maintenance of dystrophin expression and resistance to injury of skeletal muscle in gene edited DMD mice-Reference-Cited by-同舟云学术

Long-term maintenance of dystrophin expression and resistance to injury of skeletal muscle in gene edited DMD mice

Published:2022-06 Issue: Volume:28 Page:154-167
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Karri Dileep R.^ORCID,Zhang Yu^ORCID,Chemello Francesco^ORCID,Min Yi-Li,Huang Jian,Kim Jiwoong,Mammen Pradeep P.A.^ORCID,Xu Lin,Liu Ning,Bassel-Duby Rhonda^ORCID,Olson Eric N.^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference46 articles.

1. Dystrophin: the protein product of the Duchenne muscular dystrophy locus;Hoffman;Cell,1987

2. Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches;Fairclough;Nat. Rev. Genet.,2013

3. Absence of Dystrophin disrupts skeletal muscle signaling: roles of Ca2+, reactive oxygen species, and nitric oxide in the development of muscular dystrophy;Allen;Physiol. Rev.,2016

4. Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy;Amoasii;Sci. Transl Med.,2017

5. Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy;Amoasii;Science,2018

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