Lipid nanoparticle delivery limits antisense oligonucleotide activity and cellular distribution in the brain after intracerebroventricular injection-Reference-Cited by-同舟云学术

Lipid nanoparticle delivery limits antisense oligonucleotide activity and cellular distribution in the brain after intracerebroventricular injection

Published:2023-06 Issue: Volume:32 Page:773-793
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Byrnes Amy E.^ORCID,Dominguez Sara L.,Yen Chun-Wan,Laufer Benjamin I.,Foreman Oded,Reichelt Mike,Lin Han,Sagolla Meredith,Hötzel Kathy,Ngu Hai,Soendergaard Christoffer,Estevez Alberto,Lin Hsiu-Chao,Goyon Alexandre,Bian Juan,Lin Jessica,Hinz Flora I.,Friedman Brad A.,Easton Amy,Hoogenraad Casper C.^ORCID

Funder

Genentech Inc

Roche

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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