Identifying and Avoiding tcDNA-ASO Sequence-Specific Toxicity for the Development of DMD Exon 51 Skipping Therapy-Reference-Cited by-同舟云学术

Identifying and Avoiding tcDNA-ASO Sequence-Specific Toxicity for the Development of DMD Exon 51 Skipping Therapy

Published:2020-03 Issue: Volume:19 Page:371-383
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Aupy Philippine,Echevarría Lucía,Relizani Karima,Zarrouki Faouzi,Haeberli Adrian,Komisarski Marek,Tensorer Thomas,Jouvion Grégory,Svinartchouk Fedor,Garcia Luis,Goyenvalle Aurélie

Funder

Agence nationale de la recherche

Institut National de la santé et la recherche médicale

Association Monegasque contre les myopathies

Duchenne Parent project France

Fondation UVSQ

Fondation pour la Recherche Médicale

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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