One-Step Biallelic and Scarless Correction of a β-Thalassemia Mutation in Patient-Specific iPSCs without Drug Selection-Reference-Cited by-同舟云学术

One-Step Biallelic and Scarless Correction of a β-Thalassemia Mutation in Patient-Specific iPSCs without Drug Selection

Published:2017-03 Issue: Volume:6 Page:57-67
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Liu Yali,Yang Yi,Kang Xiangjin,Lin Bin,Yu Qian,Song Bing,Gao Ge,Chen Yaoyong,Sun Xiaofang,Li Xiaoping,Bu Lei,Fan Yong

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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4. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia;Cavazzana-Calvo;Nature,2010

5. Gene therapy: therapeutic gene causing lymphoma;Woods;Nature,2006

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