Reduction of Fmr1 mRNA Levels Rescues Pathological Features in Cortical Neurons in a Model of FXTAS-Reference-Cited by-同舟云学术

Reduction of Fmr1 mRNA Levels Rescues Pathological Features in Cortical Neurons in a Model of FXTAS

Published:2019-12 Issue: Volume:18 Page:546-553
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Drozd Malgorzata,Delhaye Sébastien,Maurin Thomas,Castagnola Sara,Grossi Mauro,Brau Frédéric,Jarjat Marielle,Willemsen Rob,Capovilla Maria,Hukema Renate K.,Lalli Enzo,Bardoni Barbara

Funder

CNRS

INSERM

Association Française contre les Myopathies

Fondation Recherche Médicale

Fondation Recherche sur le Cerveau

Agence Nationale de la Recherche

LabEx “Signalife” Program

MRES

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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4. Mouse models of the fragile X premutation and fragile X-associated tremor/ataxia syndrome;Berman;J. Neurodev. Disord.,2014

5. CGG Repeat-Associated Non-AUG Translation utilizes a cap-dependent scanning mechanism of initiation to produce toxic proteins;Kearse;Mol. Cell,2016

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