Natural Exon Skipping Sets the Stage for Exon Skipping as Therapy for Dystrophic Epidermolysis Bullosa-Reference-Cited by-同舟云学术

Natural Exon Skipping Sets the Stage for Exon Skipping as Therapy for Dystrophic Epidermolysis Bullosa

Published:2019-12 Issue: Volume:18 Page:465-475
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Bremer Jeroen,van der Heijden Elisabeth H.,Eichhorn Daryll S.,Meijer Rowdy,Lemmink Henny H.,Scheffer Hans,Sinke Richard J.,Jonkman Marcel F.,Pasmooij Anna M.G.,Van den Akker Peter C.

Funder

Netherlands Organisation for Health Research and Development

Clinical Fellowship

Priority Medicines Rare Disease

Dutch Butterfly Child Foundation

COST Action BM1207

COST Action CA17103

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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3. Extracutaneous manifestations and complications of inherited epidermolysis bullosa: part I. Epithelial associated tissues;Fine;J. Am. Acad. Dermatol.,2009

4. Progress toward Treatment and Cure of Epidermolysis Bullosa: Summary of the DEBRA International Research Symposium EB2015;Uitto;J. Invest. Dermatol.,2016

5. The structure and function of type VII collagen;Burgeson;Ann. N Y Acad. Sci.,1990

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