Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models-Reference-Cited by-同舟云学术

Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models

Published:2017-06 Issue: Volume:7 Page:200-210
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Moore Lauren R.,Rajpal Gautam,Dillingham Ian T.,Qutob Maya,Blumenstein Kate G.,Gattis Danielle,Hung Gene,Kordasiewicz Holly B.,Paulson Henry L.,McLoughlin Hayley S.

Funder

Ionis Pharmaceuticals

National Ataxia Foundation

NIH National Center for Advancing Translational Sciences

Michigan Brain Initiative

Becky Babcox Fund

NIH

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference39 articles.

1. Toward understanding Machado-Joseph disease;Costa;Prog. Neurobiol.,2012

2. Allele-specific RNA silencing of mutant ataxin-3 mediates neuroprotection in a rat model of Machado-Joseph disease;Alves;PLoS ONE,2008

3. Toward RNAi therapy for the polyglutamine disease Machado-Joseph disease;Costa;Mol. Ther.,2013

4. Silencing mutant ATXN3 expression resolves molecular phenotypes in SCA3 transgenic mice;Rodriguez-Lebron;Mol. Ther.,2013

5. Silencing mutant ataxin-3 rescues motor deficits and neuropathology in Machado-Joseph disease transgenic mice;Nóbrega;PLoS ONE,2013

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