Modified lentiviral globin gene therapy for pediatric β0/β0 transfusion-dependent β-thalassemia: A single-center, single-arm pilot trial
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Published:2024-07
Issue:7
Volume:31
Page:961-973.e8
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ISSN:1934-5909
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Container-title:Cell Stem Cell
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language:en
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Short-container-title:Cell Stem Cell
Author:
Li Shiqi,
Ling Sikai,
Wang Dawei,
Wang Xiaoyuan,
Hao Fangyuan,
Yin Liufan,
Yuan Zhongtao,
Liu Lin,
Zhang Lin,
Li Yu,
Chen Yingnian,
Luo Le,
Dai Ying,
Zhang Lihua,
Chen Lvzhe,
Deng Dongjie,
Tang Wei,
Zhang Sujiang,
Wang Sanbin,
Cai YujiaORCID