Efficient therapy for refractory Pompe disease by mannose 6-phosphate analogue grafting on acid α-glucosidase-Reference-Cited by-同舟云学术

Efficient therapy for refractory Pompe disease by mannose 6-phosphate analogue grafting on acid α-glucosidase

Published:2018-01 Issue: Volume:269 Page:15-23
ISSN:0168-3659
Container-title:Journal of Controlled Release
language:en
Short-container-title:Journal of Controlled Release

Author:

Basile Ilaria,Da Silva Afitz,El Cheikh Khaled,Godefroy Anastasia,Daurat Morgane,Harmois Alice,Perez Marc,Caillaud Catherine,Charbonné Henry-Vincent,Pau Bernard,Gary-Bobo Magali,Morère Alain,Garcia Marcel,Maynadier Marie

Funder

Agence Nationale de la Recherche

French Ministère de l'Enseignement supérieur, de la Recherche et de l'Innovation for Crea-Dev

Université de Montpellier

Vaincre les Maladies Lysosomales-Suisse

CNRS

NanoMedSyn

Transferts

Publisher

Elsevier BV

Subject

Pharmaceutical Science

Reference33 articles.

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2. Enzyme replacement therapy in late-onset Pompe disease: a systematic literature review;Toscano;J. Neurol.,2013

3. Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease;Kishnani;Neurology,2007

4. A randomized study of alglucosidase alfa in late-onset Pompe's disease;van der Ploeg;N. Engl. J. Med.,2010

5. Therapeutic approaches in glycogen storage disease type II/Pompe disease;Schoser;Neurotherapeutics,2008

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