Exploring the potential of natural history studies for rare neurological diseases-Reference-Cited by-同舟云学术

Exploring the potential of natural history studies for rare neurological diseases

Published:2024-07-08 Issue:9 Volume:86 Page:4947-4949
ISSN:2049-0801
Container-title:Annals of Medicine & Surgery
language:en
Short-container-title:

Author:

Muili Abdulbasit Opeyemi¹,Gomez Alejandro²,Sulaiman Ahmad Olohuntobi³,Mutata Salem⁴,Akhunji Mohammad Tufel⁵,Teemer Amadi⁶,Shahzad Akmal⁷,Kuol Piel Panther⁸

Affiliation:

1. Department of Medicine, Ladoke Akintola University of Technology, Nigeria

2. School of Medicine, Universidad Autónoma de Guadalajara, Guadalajara, Jalisco, Mexico

3. Department of Medicine and Surgery, University of Ilorin, Ilorin

4. Biology Department, Georgia State University, Georgia, USA

5. Hemchandracharya North Gujarat University

6. Neuroscience Institute, Georgia State University, Atlanta Georgia

7. The Aga Khan University Karachi, Pakistan

8. Moi University, School of Medicine, Kenya

Publisher

Ovid Technologies (Wolters Kluwer Health)

Reference7 articles.

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2. Establishing a natural history of X-linked dystonia-parkinsonism;Acuna;Brain Commun,2023

3. Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study;Nickel;Lancet Child Adolesc Health,2018

4. Study of intraventricular cerliponase alfa for CLN2 disease;Schulz;N Engl J Med,2018

5. Natural history studies in NCL and their expanding role in drug development: experiences from CLN2 disease and relevance for clinical trials;Nickel;Front Neurol,2022