A Step Toward Liver Gene Therapy: Efficient Correction of the Genetic Defect of Hepatocytes Isolated From a Patient With Crigler-Najjar Syndrome Type 1 With Lentiviral Vectors-Reference-Cited by-同舟云学术

A Step Toward Liver Gene Therapy: Efficient Correction of the Genetic Defect of Hepatocytes Isolated From a Patient With Crigler-Najjar Syndrome Type 1 With Lentiviral Vectors

Published:2009-04-15 Issue:7 Volume:87 Page:1006-1012
ISSN:0041-1337
Container-title:Transplantation
language:en
Short-container-title:

Author:

Birraux Jacques,Menzel Olivier,Wildhaber Barbara,Jond Caty,Nguyen Tuan Huy,Chardot Christophe

Publisher

Ovid Technologies (Wolters Kluwer Health)

Subject

Transplantation

Reference36 articles.

1. Treatment of the Crigler-Najjar syndrome type I with hepatocyte transplantation.;Fox;N Engl J Med,1998

2. Isolated hepatocyte transplantation in an infant with a severe urea cycle disorder.;Horslen;Pediatrics,2003

3. A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolemia.;Grossman;Nat Med,1995

4. Liver gene therapy: Advances and hurdles.;Nguyen;Gene Ther,2004

5. Highly efficient lentiviral vector-mediated transduction of nondividing, fully reimplantable primary hepatocytes.;Nguyen;Mol Ther,2002

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