Stem Cell–Mediated Transfer of a Human Artificial Chromosome Ameliorates Muscular Dystrophy-Reference-Cited by-同舟云学术

Stem Cell–Mediated Transfer of a Human Artificial Chromosome Ameliorates Muscular Dystrophy

Published:2011-08-17 Issue:96 Volume:3 Page:
ISSN:1946-6234
Container-title:Science Translational Medicine
language:en
Short-container-title:Sci. Transl. Med.

Author:

Tedesco Francesco Saverio¹²,Hoshiya Hidetoshi¹,D’Antona Giuseppe³,Gerli Mattia F. M.¹,Messina Graziella¹⁴,Antonini Stefania¹,Tonlorenzi Rossana¹,Benedetti Sara¹⁵,Berghella Libera⁶,Torrente Yvan⁷,Kazuki Yasuhiro⁸,Bottinelli Roberto³⁹,Oshimura Mitsuo⁸,Cossu Giulio¹⁴

Affiliation:

1. Division of Regenerative Medicine, Stem Cells and Gene Therapy, San Raffaele Scientific Institute, 20132 Milan, Italy.

2. Vita-Salute San Raffaele University, 20132 Milan, Italy.

3. Department of Physiology and Interuniversity Institute of Myology, University of Pavia, 27100 Pavia, Italy.

4. Department of Biology, University of Milan, 20133 Milan, Italy.

5. Department of Histology and Medical Embryology, “Sapienza” University of Rome, 00161 Rome, Italy.

6. Casa di Cura San Raffaele, 67039 Sulmona, L’Aquila, Italy.

7. Department of Neurological Science, University of Milan, Fondazione Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Policlinico Mangiagalli-Regina Elena, 20122 Milan, Italy.

8. Department of Biomedical Science, Institute of Regenerative Medicine and Biofunction, Tottori University, Yonago 683-8503, Japan.

9. Fondazione Salvatore Maugeri (IRCCS), Scientific Institute of Pavia, 27100 Pavia, Italy.

Abstract

Combining gene delivery using a human artificial chromosome with stem cell transplantation ameliorates muscular dystrophy in a mouse model.

Publisher

American Association for the Advancement of Science (AAAS)

Subject

General Medicine

Reference47 articles.

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3. The muscular dystrophies

4. A. E. Emery F. Muntoni Duchenne Muscular Dystrophy (Oxford Univ. Press Oxford UK ed. 3 2003).

5. Repairing skeletal muscle: regenerative potential of skeletal muscle stem cells

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