Therapeutic targeting of the RB1 pathway in retinoblastoma with the oncolytic adenovirus VCN-01

Author:

Pascual-Pasto Guillem12ORCID,Bazan-Peregrino Miriam3ORCID,Olaciregui Nagore G.12,Restrepo-Perdomo Camilo A.4,Mato-Berciano Ana3,Ottaviani Daniela56,Weber Klaus7ORCID,Correa Genoveva12,Paco Sonia12,Vila-Ubach Monica12,Cuadrado-Vilanova Maria12,Castillo-Ecija Helena12ORCID,Botteri Gaia12ORCID,Garcia-Gerique Laura12,Moreno-Gilabert Helena12ORCID,Gimenez-Alejandre Marta3,Alonso-Lopez Patricia3,Farrera-Sal Marti3ORCID,Torres-Manjon Silvia8,Ramos-Lozano Dolores8,Moreno Rafael8ORCID,Aerts Isabelle56,Doz François59ORCID,Cassoux Nathalie5910ORCID,Chapeaublanc Elodie56ORCID,Torrebadell Montserrat12ORCID,Roldan Monica14,König Andrés11,Suñol Mariona4,Claverol Joana112,Lavarino Cinzia12,Carmen de Torres12,Fu Ligia13,Radvanyi François56,Munier Francis L.14,Catalá-Mora Jaume15ORCID,Mora Jaume12,Alemany Ramón8,Cascalló Manel3,Chantada Guillermo L.121617ORCID,Carcaboso Angel M.12ORCID

Affiliation:

1. Institut de Recerca Sant Joan de Deu, Barcelona 08950, Spain.

2. Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, Barcelona 08950, Spain.

3. VCN Biosciences, Sant Cugat del Valles, Barcelona 08174, Spain.

4. Pathology, Hospital Sant Joan de Deu, Barcelona 08950, Spain.

5. Institut Curie, CNRS, UMR144, SIREDO Oncology Center, 75248 Paris, France.

6. Institut Curie, PSL Research University, 75248 Paris, France.

7. AnaPath GmbH, Oberbuchsiten 4625, Switzerland.

8. Translational Research Laboratory, IDIBELL-Institut Catala d’Oncologia, 08908, L’Hospitalet de Llobregat, Barcelona, Spain.

9. Paris Descartes University, 75006 Paris, France.

10. Institut Curie, Ophthalmic Oncology, 75248 Paris, France.

11. Vivotecnia Research S.L., Tres Cantos, Madrid 28760, Spain.

12. Clinical Trials Unit, Hospital Sant Joan de Deu, Barcelona 08950, Spain.

13. Pediatric Hematology-Oncology, Hospital Escuela Universitario, Tegucigalpa, Honduras.

14. Hôpital Ophtalmique Jules-Gonin, Lausanne 133, Switzerland.

15. Ophthalmology, Hospital Sant Joan de Deu, Barcelona 08950, Spain.

16. Hospital de Pediatria JP Garrahan, Buenos Aires 1245, Argentina.

17. CONICET, Buenos Aires 1245, Argentina.

Abstract

An oncolytic adenovirus shows antitumor efficacy in patient-derived models of intraocular retinoblastoma and appears safe for human use.

Funder

Seventh Framework Programme

Institut national de la santé et de la recherche médicale

Fundación Científica Asociación Española Contra el Cáncer

Instituto de Salud Carlos III

Institut National Du Cancer

Ministerio de Economía, Industria y Competitividad, Gobierno de España

Publisher

American Association for the Advancement of Science (AAAS)

Subject

General Medicine

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