Hemophilia as a blueprint for gene therapy
Author:
Affiliation:
1. Division of Hematology/Oncology, Department of Medicine, University of Pittsburgh Medical Center, Pittsburgh, PA, USA.
2. Hemophilia Center of Western PA, Pittsburgh, PA, USA.
Abstract
Publisher
American Association for the Advancement of Science (AAAS)
Subject
Multidisciplinary
Reference15 articles.
1. Emicizumab Prophylaxis in Hemophilia A with Inhibitors
2. Subcutaneous concizumab prophylaxis in hemophilia A and hemophilia A/B with inhibitors: phase 2 trial results
3. Targeting of Antithrombin in Hemophilia A or B with RNAi Therapy
4. Emicizumab, a bispecific antibody recognizing coagulation factors IX and X: how does it actually compare to factor VIII?
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