1. FDA: Human Gene Therapy for Neurodegenerative Diseases. Draft Guidance for Industry. https://www.fda.gov/media/144886/download (2021). Accessed 2022.
2. FDA: Human Gene Therapy for Hemophilia Guidance for Industry. https://www.fda.gov/media/113799/download (2020). Accessed.
3. FDA: Human Gene Therapy for Rare Diseases Guidance for Industry. https://www.fda.gov/media/113807/downlod (2020). Accessed.
4. FDA: Human Gene Therapy for Retinal Disorders Guidance for Industry. https://www.fda.gov/media/124641/download (2020). Accessed.
5. Takeuchi A, Saito T. CD4 CTL, a cytotoxic subset of CD4(+) T cells, their differentiation and function. Front Immunol. 2017;8:194. https://doi.org/10.3389/fimmu.2017.00194.