Effects of Lumacaftor–Ivacaftor Therapy on Cystic Fibrosis Transmembrane Conductance Regulator Function in Phe508del Homozygous Patients with Cystic Fibrosis

Author:

Graeber Simon Y.1234,Dopfer Christian56,Naehrlich Lutz78,Gyulumyan Lena5,Scheuermann Heike1,Hirtz Stephanie1,Wege Sabine9,Mairbäurl Heimo3910,Dorda Marie56,Hyde Rebecca56,Bagheri-Hanson Azadeh7,Rueckes-Nilges Claudia78,Fischer Sebastian56,Mall Marcus A.1234,Tümmler Burkhard56

Affiliation:

1. Department of Translational Pulmonology

2. Division of Pediatric Pulmonology and Allergy and Cystic Fibrosis Center, Department of Pediatrics, and

3. Translational Lung Research Center Heidelberg, German Center for Lung Research, University of Heidelberg, Heidelberg, Germany

4. Department of Pediatric Pulmonology and Immunology and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, Berlin, Germany

5. Clinic of Pediatric Pneumology, Allergology, and Neonatology and

6. Biomedical Research in Endstage and Obstructive Lung Disease Hannover, German Center for Lung Research, Hannover Medical School, Hannover, Germany

7. Department of Pediatrics, Justus-Liebig-University Giessen, Giessen, Germany

8. Universities of Giessen and Marburg Lung Center, German Center for Lung Research, Giessen, Germany

9. Department of Pneumology and Respiratory Critical Care Medicine, Thoraxklinik, University Hospital Heidelberg, Heidelberg, Germany; and

10. Medical Clinic VII, Sports Medicine, Heidelberg University Hospital, Heidelberg, Germany

Publisher

American Thoracic Society

Subject

Critical Care and Intensive Care Medicine,Pulmonary and Respiratory Medicine

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