Clinical Effectiveness of Elexacaftor/Tezacftor/Ivacaftor in People with Cystic Fibrosis

Author:

Nichols David P12ORCID,Paynter Alex C3,Heltshe Sonya L.45,Donaldson Scott H6,Frederick Carla A7,Freedman Steven D.8,Gelfond Daniel9,Hoffman Lucas R.1011,Kelly Andrea12,Narkewicz Michael R13,Pittman Jessica E.14,Ratjen Felix15,Rosenfeld Margaret16,Sagel Scott D17ORCID,Schwarzenberg Sarah Jane18,Singh Pradeep K19,Solomon George M20,Stalvey Michael S21,Clancy John P2223,Kirby Shannon3,Van Dalfsen Jill M.24,Kloster Margaret H.4,Rowe Steven M25ORCID,

Affiliation:

1. University of Washington School of Medicine, 12353, Pediatrics, Seattle, Washington, United States

2. Seattle Children's Hospital, 7274, Pediatric Pulmonology, Seattle, Washington, United States;

3. Seattle Children's Research Institute, 145793, Seattle, Washington, United States

4. Seattle Children's Research Institute, Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle, Washington, United States

5. University of Washington School of Medicine, Pediatrics, Seattle, Washington, United States

6. UNC, Medicine, Chapel Hill, North Carolina, United States

7. University at Buffalo Jacobs School of Medicine and Biomedical Sciences, 12291, Buffalo, New York, United States

8. Beth Israel Deaconess Medical Center, Gastroenterology, Boston, Massachusetts, United States

9. Western New York Pediatric Gastroenterology, Batavia, New York, United States

10. University of Washington School of Medicine, 12353, Seattle, Washington, United States

11. Seattle Children's Hospital, 7274, Seattle, Washington, United States

12. The Children's Hospital of Philadelphia, 6567, Pediatrics, Division of Endocrinology & Diabetes, Philadelphia, Pennsylvania, United States

13. Children's Hospital Colorado and University of Colorado School of Medicine, Digestive Health Institute and Pediatrics, Aurora, Colorado, United States

14. Washington University in Saint Louis School of Medicine, 12275, Department of Pediatrics, Saint Louis, Missouri, United States

15. University of Toronto HSC, Division of Respiratory Medicine, Toronto, Ontario, Canada

16. Seattle Children's, Pediatrics / Pulmonary, Seattle, Washington, United States

17. University of Colorado School of Medicine, Pediatrics, Aurora, Colorado, United States

18. University of Minnesota Masonic Children's Hospital, 501779, Pediatrics, Minneapolis, Minnesota, United States

19. University of Washington, 7284, Department of Microbiology and Medicine, Seattle, Washington, United States

20. University of Alabama at Birmingham, 9968, Medicine, Gregory Fleming James Cystic Fibrosis Research Center, Birmingham, Alabama, United States

21. The University of Alabama at Birmingham School of Medicine, 9967, Birmingham, Alabama, United States

22. Cincinnati Children's Hospital Medical Center, 2518, Department of Pediatrics, Cincinnati, Ohio, United States

23. Cincinnati Children's Hospital Medical Center, 2518, Division of Pulmonary Medicine, Cincinnati, Ohio, United States

24. Cystic Fibrosis Foundation Therapeutics Development Network Coordinating Center, Seattle Children’s Research Institute, Seattle, Washington, United States

25. University of Alabama at Birmingham, Medicine, Cystic Fibrosis Center, Birmingham, Alabama, United States

Publisher

American Thoracic Society

Subject

Critical Care and Intensive Care Medicine,Pulmonary and Respiratory Medicine

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