Effects of Elexacaftor/Tezacaftor/Ivacaftor Therapy on CFTR Function in Patients with Cystic Fibrosis and One or Two F508del Alleles

Author:

Graeber Simon Y.123ORCID,Vitzthum Constanze13,Pallenberg Sophia T.45,Naehrlich Lutz67,Stahl Mirjam123ORCID,Rohrbach Alexander1,Drescher Marika13,Minso Rebecca4,Ringshausen Felix C85,Rueckes-Nilges Claudia6,Klajda Jan6,Berges Julian910,Yu Yin911,Scheuermann Heike910,Hirtz Stephanie910,Sommerburg Olaf910,Dittrich Anna-Maria45ORCID,Tümmler Burkhard45,Mall Marcus A1212ORCID

Affiliation:

1. Charité Universitätsmedizin Berlin, 14903, Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Berlin, Germany

2. Berlin Institute of Health, 522475, Berlin, Germany

3. German Center for Lung Research, 542891, associated partner, Berlin, Germany

4. Hannover Medical School, 9177, Department of Pediatric Pneumology, Allergology and Neonatology, Hannover, Germany

5. German Center for Lung Research, 542891, Biomedical Research in Endstage and Obstructive Lung Disease Hannover (BREATH), Hannover, Germany

6. Justus-Liebig-University Giessen, Department of Pediatrics, Giessen, Germany

7. German Center for Lung Research, 542891, Universities of Giessen and Marburg Lung Center (UGMLC), Giessen, Germany

8. Hannover Medical School, 9177, Department of Respiratory Medicine, Hannover, Germany

9. University of Heidelberg, 9144, Department of Pediatrics, Division of Pediatric Pulmonology and Allergy and Cystic Fibrosis Center, Heidelberg, Germany

10. University of Heidelberg, 9144, Department of Translational Pulmonology, Translational Lung Research Center Heidelberg (TLRC), German Center for Lung Research (DZL), Heidelberg, Germany

11. University of Heidelberg, 9144, German Centre for Lung Research (DZL), Translational Lung Research Center Heidelberg (TLRC), Department of Translational Pulmonology, Heidelberg, Germany

12. German Center for Lung Research, 542891, associated partner, Berlin, Germany;

Publisher

American Thoracic Society

Subject

Critical Care and Intensive Care Medicine,Pulmonary and Respiratory Medicine

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