Targeted inversion and reversion of the blood coagulation factor 8 gene in human iPS cells using TALENs
Author:
Publisher
Proceedings of the National Academy of Sciences
Subject
Multidisciplinary
Reference55 articles.
1. Haemophilia A: from mutation analysis to new therapies
2. Haemophilias A and B
3. Inversions disrupting the factor VIII gene are a common cause of severe haemophilia A
4. Characteristic mRNA abnormality found in half the patients with severe haemophilia A is due to large DNA inversions
5. Recurrent inversion breaking intron 1 of the factor VIII gene is a frequent cause of severe hemophilia A
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