Sustained correction of bleeding disorder in hemophilia B mice by gene therapy
Author:
Publisher
Proceedings of the National Academy of Sciences
Subject
Multidisciplinary
Reference22 articles.
1. A Coagulation Factor IX-Deficient Mouse Model for Human Hemophilia B
2. A factor IX-deficient mouse model for hemophilia B gene therapy
3. Targeted Inactivation of the Coagulation Factor IX Gene Causes Hemophilia B in Mice
4. Human Factor IX Corrects the Bleeding Diathesis of Mice With Hemophilia B
5. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
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